Memantine, a long-approved and cost-effective drug used to treat Alzheimer’s disease, could also benefit patients with sickle cell anemia in the future. Initial clinical data from an international ...

SCD gene therapy approaches using CRISPR, gene therapy, and base editing show different stem cell outcomes in a mouse study.

A 21-year-old man has become the first person in New York—and one of the first in the world—to be cured of sickle cell anemia. A novel form of gene therapy enabled the man to receive a life-changing ...